HK1185098A1 - 高效跳過裘馨氏肌肉營養不良症前體 外顯子 的方法和工具 - Google Patents

高效跳過裘馨氏肌肉營養不良症前體 外顯子 的方法和工具

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Publication number
HK1185098A1
HK1185098A1 HK13112417.5A HK13112417A HK1185098A1 HK 1185098 A1 HK1185098 A1 HK 1185098A1 HK 13112417 A HK13112417 A HK 13112417A HK 1185098 A1 HK1185098 A1 HK 1185098A1
Authority
HK
Hong Kong
Prior art keywords
mrna
exon
methods
muscular dystrophy
duchenne muscular
Prior art date
Application number
HK13112417.5A
Other languages
English (en)
Inventor
Johannes De Kimpe Josephus
Johannes Platenburg Gerardus
Christina Theodora Van Deutekom Judith
Aartsma-Rus Annemieke
Boudewijn Van Ommen Garrit-Jan
Original Assignee
Biomarin Tech Bv
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Filing date
Publication date
Family has litigation
First worldwide family litigation filed litigation Critical https://patents.darts-ip.com/?family=39045623&utm_source=***_patent&utm_medium=platform_link&utm_campaign=public_patent_search&patent=HK1185098(A1) "Global patent litigation dataset” by Darts-ip is licensed under a Creative Commons Attribution 4.0 International License.
Application filed by Biomarin Tech Bv filed Critical Biomarin Tech Bv
Publication of HK1185098A1 publication Critical patent/HK1185098A1/zh

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HK13112417.5A 2007-10-26 2012-01-16 高效跳過裘馨氏肌肉營養不良症前體 外顯子 的方法和工具 HK1185098A1 (zh)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
EP07119351 2007-10-26
PCT/NL2008/050673 WO2009054725A2 (en) 2007-10-26 2008-10-27 Means and methods for counteracting muscle disorders

Publications (1)

Publication Number Publication Date
HK1185098A1 true HK1185098A1 (zh) 2014-02-07

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HK13112417.5A HK1185098A1 (zh) 2007-10-26 2012-01-16 高效跳過裘馨氏肌肉營養不良症前體 外顯子 的方法和工具
HK18105446.9A HK1245670A1 (zh) 2007-10-26 2018-04-26 對抗肌肉病症的裝置和方法

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HK18105446.9A HK1245670A1 (zh) 2007-10-26 2018-04-26 對抗肌肉病症的裝置和方法

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US (18) US9243245B2 (zh)
EP (4) EP2614827B1 (zh)
JP (6) JP5600064B2 (zh)
CN (5) CN105641700B (zh)
AU (1) AU2008317566B2 (zh)
CA (1) CA2704049A1 (zh)
CY (2) CY1117286T1 (zh)
DK (1) DK2203173T3 (zh)
ES (5) ES2639852T3 (zh)
HK (2) HK1185098A1 (zh)
HR (1) HRP20160025T1 (zh)
HU (2) HUE028662T2 (zh)
IL (4) IL205322A (zh)
NZ (2) NZ584793A (zh)
PL (1) PL2203173T3 (zh)
PT (1) PT2203173E (zh)
WO (1) WO2009054725A2 (zh)

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EP1191097A1 (en) * 2000-09-21 2002-03-27 Leids Universitair Medisch Centrum Induction of exon skipping in eukaryotic cells
AU2003225410A1 (en) 2003-03-21 2004-10-11 Academisch Ziekenhuis Leiden Modulation of exon recognition in pre-mrna by interfering with the secondary rna structure
SI2910551T1 (sl) 2003-04-11 2017-07-31 Ptc Therapeutics, Inc. Spojine 1,2,4-oksadiazol benzojske kisline in njihova uporaba za zatiranje nesmiselne ter zdravljenje bolezni
USRE48960E1 (en) 2004-06-28 2022-03-08 The University Of Western Australia Antisense oligonucleotides for inducing exon skipping and methods of use thereof
ES2361325T3 (es) 2004-06-28 2011-06-16 The University Of Western Australia Oligonucleótidos antisentido para inducir la omisión de exón y métodos de uso de los mismos.
AU2006213686A1 (en) 2005-02-09 2006-08-17 Avi Bio Pharma, Inc. Antisense composition and method for treating muscle atrophy
WO2008018795A1 (en) 2006-08-11 2008-02-14 Prosensa Technologies B.V. Methods and means for treating dna repeat instability associated genetic disorders
NZ584793A (en) 2007-10-26 2012-05-25 Academisch Ziekenhuis Leiden Means and methods for counteracting muscle disorders
EP2119783A1 (en) * 2008-05-14 2009-11-18 Prosensa Technologies B.V. Method for efficient exon (44) skipping in Duchenne Muscular Dystrophy and associated means
US8084601B2 (en) 2008-09-11 2011-12-27 Royal Holloway And Bedford New College Royal Holloway, University Of London Oligomers
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AU2008317566B2 (en) 2014-05-01
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US20210139904A1 (en) 2021-05-13
JP2021113229A (ja) 2021-08-05
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