MX2022003585A - Metodos para tratar hiperfenilalaninemia. - Google Patents

Metodos para tratar hiperfenilalaninemia.

Info

Publication number
MX2022003585A
MX2022003585A MX2022003585A MX2022003585A MX2022003585A MX 2022003585 A MX2022003585 A MX 2022003585A MX 2022003585 A MX2022003585 A MX 2022003585A MX 2022003585 A MX2022003585 A MX 2022003585A MX 2022003585 A MX2022003585 A MX 2022003585A
Authority
MX
Mexico
Prior art keywords
methods
hyperphenylalaninemia
treating
treating hyperphenylalaninemia
sepiapterin
Prior art date
Application number
MX2022003585A
Other languages
English (en)
Inventor
Niel Smith
Original Assignee
Ptc Therapeutics Mp Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Ptc Therapeutics Mp Inc filed Critical Ptc Therapeutics Mp Inc
Publication of MX2022003585A publication Critical patent/MX2022003585A/es

Links

Classifications

    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P3/00Drugs for disorders of the metabolism
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00Medicinal preparations containing organic active ingredients
    • A61K31/33Heterocyclic compounds
    • A61K31/395Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/495Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with two or more nitrogen atoms as the only ring heteroatoms, e.g. piperazine or tetrazines
    • A61K31/505Pyrimidines; Hydrogenated pyrimidines, e.g. trimethoprim
    • A61K31/519Pyrimidines; Hydrogenated pyrimidines, e.g. trimethoprim ortho- or peri-condensed with heterocyclic rings
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/0087Galenical forms not covered by A61K9/02 - A61K9/7023
    • A61K9/0095Drinks; Beverages; Syrups; Compositions for reconstitution thereof, e.g. powders or tablets to be dispersed in a glass of water; Veterinary drenches

Landscapes

  • Health & Medical Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Medicinal Chemistry (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Animal Behavior & Ethology (AREA)
  • General Health & Medical Sciences (AREA)
  • Public Health (AREA)
  • Veterinary Medicine (AREA)
  • Epidemiology (AREA)
  • Engineering & Computer Science (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Diabetes (AREA)
  • Hematology (AREA)
  • Obesity (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • General Chemical & Material Sciences (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Organic Chemistry (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
  • Medicinal Preparation (AREA)

Abstract

La invención presenta métodos para reducir la concentración de fenilalanina en sangre en un sujeto por la administración de sepiapterina, o una sal farmacéuticamente aceptable de la misma.
MX2022003585A 2019-09-25 2020-09-25 Metodos para tratar hiperfenilalaninemia. MX2022003585A (es)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201962905720P 2019-09-25 2019-09-25
PCT/US2020/052871 WO2021062264A1 (en) 2019-09-25 2020-09-25 Methods for treating hyperphenylalaninemia

Publications (1)

Publication Number Publication Date
MX2022003585A true MX2022003585A (es) 2022-04-19

Family

ID=72827023

Family Applications (1)

Application Number Title Priority Date Filing Date
MX2022003585A MX2022003585A (es) 2019-09-25 2020-09-25 Metodos para tratar hiperfenilalaninemia.

Country Status (12)

Country Link
US (1) US20220362249A1 (es)
EP (1) EP4034122A1 (es)
JP (1) JP2022549834A (es)
KR (1) KR20220070477A (es)
CN (1) CN114650825A (es)
AU (1) AU2020353676A1 (es)
BR (1) BR112022003719A2 (es)
CA (1) CA3150003A1 (es)
IL (1) IL291565A (es)
JO (1) JOP20220042A1 (es)
MX (1) MX2022003585A (es)
WO (1) WO2021062264A1 (es)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
BR112019010222A8 (pt) 2016-11-29 2022-11-22 Censa Pharmaceuticals Inc Polimorfos de sepiapterina e sais dos mesmos
WO2019046849A1 (en) 2017-09-01 2019-03-07 Censa Pharmaceuticals Inc. PHARMACEUTICAL COMPOSITION COMPRISING SEPAPTERINE AND USES THEREOF
CN112703002A (zh) 2018-05-30 2021-04-23 Ptc医疗Mp公司 增加墨蝶呤血浆暴露的方法
US20210161901A1 (en) * 2018-05-30 2021-06-03 Ptc Therapeutics Mp, Inc. Compositions and methods for increasing tetrahydrobiopterin plasma exposure

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5910304A (en) 1982-12-13 1999-06-08 Texas A&M University System Low-dose oral administration of interferons
CA1320905C (en) 1986-11-06 1993-08-03 Joseph M. Cummins Treatment of immuno-resistant disease
US6036949A (en) 1998-03-05 2000-03-14 Amarillo Biosciences, Inc. Treatment of fibromyalgia with low doses of interferon
HUE030221T2 (en) * 2014-03-31 2017-04-28 Vasopharm Gmbh Solid pharmaceutical composition containing biopterin derivatives and uses of such compositions
BR112019010222A8 (pt) 2016-11-29 2022-11-22 Censa Pharmaceuticals Inc Polimorfos de sepiapterina e sais dos mesmos
EP3548487A4 (en) 2016-11-29 2020-04-29 Censa Pharmaceuticals Inc. POLYMORPHE SHAPE OF SEPIAPTERIN
WO2019046849A1 (en) * 2017-09-01 2019-03-07 Censa Pharmaceuticals Inc. PHARMACEUTICAL COMPOSITION COMPRISING SEPAPTERINE AND USES THEREOF
AU2019277372A1 (en) 2018-05-30 2021-01-21 Ptc Therapeutics Mp, Inc. Pharmaceutically acceptable salts of sepiapterin

Also Published As

Publication number Publication date
JOP20220042A1 (ar) 2023-01-30
EP4034122A1 (en) 2022-08-03
CA3150003A1 (en) 2021-04-01
KR20220070477A (ko) 2022-05-31
US20220362249A1 (en) 2022-11-17
CN114650825A (zh) 2022-06-21
IL291565A (en) 2022-05-01
WO2021062264A1 (en) 2021-04-01
JP2022549834A (ja) 2022-11-29
BR112022003719A2 (pt) 2022-05-31
AU2020353676A1 (en) 2022-04-14

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