SI2946785T1 - Postopek napovedovanja odziva na farmakološko zdravljenje bolezni s šaperoni - Google Patents

Postopek napovedovanja odziva na farmakološko zdravljenje bolezni s šaperoni

Info

Publication number
SI2946785T1
SI2946785T1 SI200931920T SI200931920T SI2946785T1 SI 2946785 T1 SI2946785 T1 SI 2946785T1 SI 200931920 T SI200931920 T SI 200931920T SI 200931920 T SI200931920 T SI 200931920T SI 2946785 T1 SI2946785 T1 SI 2946785T1
Authority
SI
Slovenia
Prior art keywords
diseases
pharmacological chaperone
predict response
chaperone treatment
treatment
Prior art date
Application number
SI200931920T
Other languages
English (en)
Inventor
Elfrida Benjamin
Hung V Do
Xiaoyang Wu
John Flanagan
Brandon Wustman
Original Assignee
Amicus Therapeutics, Inc.
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Family has litigation
First worldwide family litigation filed litigation Critical https://patents.darts-ip.com/?family=40957500&utm_source=***_patent&utm_medium=platform_link&utm_campaign=public_patent_search&patent=SI2946785(T1) "Global patent litigation dataset” by Darts-ip is licensed under a Creative Commons Attribution 4.0 International License.
Application filed by Amicus Therapeutics, Inc. filed Critical Amicus Therapeutics, Inc.
Publication of SI2946785T1 publication Critical patent/SI2946785T1/sl

Links

Classifications

    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00—Medicinal preparations containing organic active ingredients
    • A61K31/33—Heterocyclic compounds
    • A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/435—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
    • A61K31/44—Non condensed pyridines; Hydrogenated derivatives thereof
    • A61K31/445—Non condensed piperidines, e.g. piperocaine
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P3/00—Drugs for disorders of the metabolism
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P3/00—Drugs for disorders of the metabolism
    • A61P3/06—Antihyperlipidemics
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P3/00—Drugs for disorders of the metabolism
    • A61P3/08—Drugs for disorders of the metabolism for glucose homeostasis
    • A61P3/10—Drugs for disorders of the metabolism for glucose homeostasis for hyperglycaemia, e.g. antidiabetics
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00—Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
    • C—CHEMISTRY; METALLURGY
    • C07—ORGANIC CHEMISTRY
    • C07K—PEPTIDES
    • C07K14/00—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
    • C—CHEMISTRY; METALLURGY
    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12Q—MEASURING OR TESTING PROCESSES INVOLVING ENZYMES, NUCLEIC ACIDS OR MICROORGANISMS; COMPOSITIONS OR TEST PAPERS THEREFOR; PROCESSES OF PREPARING SUCH COMPOSITIONS; CONDITION-RESPONSIVE CONTROL IN MICROBIOLOGICAL OR ENZYMOLOGICAL PROCESSES
    • C12Q1/00—Measuring or testing processes involving enzymes, nucleic acids or microorganisms; Compositions therefor; Processes of preparing such compositions
    • C12Q1/34—Measuring or testing processes involving enzymes, nucleic acids or microorganisms; Compositions therefor; Processes of preparing such compositions involving hydrolase
    • G—PHYSICS
    • G01—MEASURING; TESTING
    • G01N—INVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
    • G01N33/00—Investigating or analysing materials by specific methods not covered by groups G01N1/00 - G01N31/00
    • G01N33/48—Biological material, e.g. blood, urine; Haemocytometers
    • G01N33/50—Chemical analysis of biological material, e.g. blood, urine; Testing involving biospecific ligand binding methods; Immunological testing
    • G01N33/68—Chemical analysis of biological material, e.g. blood, urine; Testing involving biospecific ligand binding methods; Immunological testing involving proteins, peptides or amino acids
    • G01N33/6893—Chemical analysis of biological material, e.g. blood, urine; Testing involving biospecific ligand binding methods; Immunological testing involving proteins, peptides or amino acids related to diseases not provided for elsewhere
    • G—PHYSICS
    • G01—MEASURING; TESTING
    • G01N—INVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
    • G01N2333/00—Assays involving biological materials from specific organisms or of a specific nature
    • G01N2333/435—Assays involving biological materials from specific organisms or of a specific nature from animals; from humans
    • G01N2333/46—Assays involving biological materials from specific organisms or of a specific nature from animals; from humans from vertebrates
    • G01N2333/47—Assays involving proteins of known structure or function as defined in the subgroups
    • G—PHYSICS
    • G01—MEASURING; TESTING
    • G01N—INVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
    • G01N2333/00—Assays involving biological materials from specific organisms or of a specific nature
    • G01N2333/90—Enzymes; Proenzymes
    • G01N2333/914—Hydrolases (3)
    • G01N2333/924—Hydrolases (3) acting on glycosyl compounds (3.2)
    • G01N2333/94—Hydrolases (3) acting on glycosyl compounds (3.2) acting on alpha-galactose-glycoside bonds, e.g. alpha-galactosidase
    • G—PHYSICS
    • G01—MEASURING; TESTING
    • G01N—INVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
    • G01N2800/00—Detection or diagnosis of diseases
    • G01N2800/04—Endocrine or metabolic disorders
    • G—PHYSICS
    • G01—MEASURING; TESTING
    • G01N—INVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
    • G01N2800/00—Detection or diagnosis of diseases
    • G01N2800/38—Pediatrics
    • G—PHYSICS
    • G01—MEASURING; TESTING
    • G01N—INVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
    • G01N2800/00—Detection or diagnosis of diseases
    • G01N2800/52—Predicting or monitoring the response to treatment, e.g. for selection of therapy based on assay results in personalised medicine; Prognosis

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Engineering & Computer Science (AREA)
  • Organic Chemistry (AREA)
  • General Health & Medical Sciences (AREA)
  • Medicinal Chemistry (AREA)
  • Molecular Biology (AREA)
  • Proteomics, Peptides & Aminoacids (AREA)
  • Hematology (AREA)
  • Immunology (AREA)
  • Veterinary Medicine (AREA)
  • Public Health (AREA)
  • Animal Behavior & Ethology (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Biochemistry (AREA)
  • Diabetes (AREA)
  • Physics & Mathematics (AREA)
  • Analytical Chemistry (AREA)
  • Wood Science & Technology (AREA)
  • Urology & Nephrology (AREA)
  • Microbiology (AREA)
  • Biomedical Technology (AREA)
  • Biotechnology (AREA)
  • Zoology (AREA)
  • General Chemical & Material Sciences (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Genetics & Genomics (AREA)
  • Biophysics (AREA)
  • Obesity (AREA)
  • Epidemiology (AREA)
  • Pathology (AREA)
  • General Physics & Mathematics (AREA)
  • Food Science & Technology (AREA)
  • Cell Biology (AREA)
  • General Engineering & Computer Science (AREA)
  • Gastroenterology & Hepatology (AREA)
  • Endocrinology (AREA)
SI200931920T 2008-02-12 2009-02-12 Postopek napovedovanja odziva na farmakološko zdravljenje bolezni s šaperoni SI2946785T1 (sl)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US2814108P 2008-02-12 2008-02-12
US3568408P 2008-03-11 2008-03-11
US9363108P 2008-09-02 2008-09-02
US11349608P 2008-11-11 2008-11-11
EP15162630.6A EP2946785B1 (en) 2008-02-12 2009-02-12 Method to predict response to pharmacological chaperone treatment of diseases

Publications (1)

Publication Number Publication Date
SI2946785T1 true SI2946785T1 (sl) 2019-02-28

Family

ID=40957500

Family Applications (3)

Application Number Title Priority Date Filing Date
SI200931229T SI2252313T1 (sl) 2008-02-12 2009-02-12 Postopek napovedovanja odgovora na zdravljenje bolezni s farmakološkim spremljevalcem
SI200932099T SI3470077T1 (sl) 2008-02-12 2009-02-12 Postopek za napovedovanje odgovora na zdravljenje bolezni s farmakološkim spremljevalcem
SI200931920T SI2946785T1 (sl) 2008-02-12 2009-02-12 Postopek napovedovanja odziva na farmakološko zdravljenje bolezni s šaperoni

Family Applications Before (2)

Application Number Title Priority Date Filing Date
SI200931229T SI2252313T1 (sl) 2008-02-12 2009-02-12 Postopek napovedovanja odgovora na zdravljenje bolezni s farmakološkim spremljevalcem
SI200932099T SI3470077T1 (sl) 2008-02-12 2009-02-12 Postopek za napovedovanje odgovora na zdravljenje bolezni s farmakološkim spremljevalcem

Country Status (16)

Country Link
US (8) US8592362B2 (sl)
EP (4) EP3470077B1 (sl)
JP (6) JP5844045B2 (sl)
AU (6) AU2009214648B2 (sl)
CA (1) CA2715407C (sl)
CY (3) CY1116466T1 (sl)
DK (3) DK2252313T3 (sl)
ES (3) ES2541933T3 (sl)
HR (3) HRP20150728T1 (sl)
HU (3) HUE051377T2 (sl)
LT (2) LT3470077T (sl)
MX (1) MX2010008835A (sl)
PL (3) PL3470077T3 (sl)
PT (3) PT3470077T (sl)
SI (3) SI2252313T1 (sl)
WO (1) WO2009102895A2 (sl)

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Also Published As

Publication number Publication date
JP2023109807A (ja) 2023-08-08
MX2010008835A (es) 2010-10-20
JP7277493B2 (ja) 2023-05-19
CY1121386T1 (el) 2020-05-29
EP2252313A4 (en) 2011-04-13
HUE051377T2 (hu) 2021-03-01
US20190000818A1 (en) 2019-01-03
JP2019088289A (ja) 2019-06-13
PT3470077T (pt) 2020-11-30
AU2014221321A1 (en) 2014-10-02
AU2021218172A1 (en) 2021-10-07
EP3470077A1 (en) 2019-04-17
HRP20150728T1 (hr) 2015-08-14
ES2836121T3 (es) 2021-06-24
AU2009214648A1 (en) 2009-08-20
EP2252313A2 (en) 2010-11-24
PL2252313T3 (pl) 2015-09-30
LT2946785T (lt) 2019-02-11
SI2252313T1 (sl) 2015-08-31
AU2019219727B2 (en) 2021-05-20
JP2011514152A (ja) 2011-05-06
US8592362B2 (en) 2013-11-26
JP6837469B2 (ja) 2021-03-03
US9095584B2 (en) 2015-08-04
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