BR112022005895A2 - Inibidores de aldose redutase para tratamento de deficiência de fosfomanomutase 2 - Google Patents
Inibidores de aldose redutase para tratamento de deficiência de fosfomanomutase 2Info
- Publication number
- BR112022005895A2 BR112022005895A2 BR112022005895A BR112022005895A BR112022005895A2 BR 112022005895 A2 BR112022005895 A2 BR 112022005895A2 BR 112022005895 A BR112022005895 A BR 112022005895A BR 112022005895 A BR112022005895 A BR 112022005895A BR 112022005895 A2 BR112022005895 A2 BR 112022005895A2
- Authority
- BR
- Brazil
- Prior art keywords
- aldose
- inhibitors
- phosphomanomutase
- redutase
- deficiency
- Prior art date
Links
Classifications
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/33—Heterocyclic compounds
- A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
- A61K31/495—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with two or more nitrogen atoms as the only ring heteroatoms, e.g. piperazine or tetrazines
- A61K31/50—Pyridazines; Hydrogenated pyridazines
- A61K31/5025—Pyridazines; Hydrogenated pyridazines ortho- or peri-condensed with heterocyclic ring systems
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P25/00—Drugs for disorders of the nervous system
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P3/00—Drugs for disorders of the metabolism
Landscapes
- Health & Medical Sciences (AREA)
- Chemical & Material Sciences (AREA)
- Medicinal Chemistry (AREA)
- Pharmacology & Pharmacy (AREA)
- Life Sciences & Earth Sciences (AREA)
- Animal Behavior & Ethology (AREA)
- General Health & Medical Sciences (AREA)
- Public Health (AREA)
- Veterinary Medicine (AREA)
- Epidemiology (AREA)
- Organic Chemistry (AREA)
- General Chemical & Material Sciences (AREA)
- Engineering & Computer Science (AREA)
- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
- Bioinformatics & Cheminformatics (AREA)
- Chemical Kinetics & Catalysis (AREA)
- Neurosurgery (AREA)
- Neurology (AREA)
- Biomedical Technology (AREA)
- Diabetes (AREA)
- Hematology (AREA)
- Obesity (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Enzymes And Modification Thereof (AREA)
Abstract
A presente invenção refere-se a métodos para tratar PMM2-CDG com o uso de inibidores de aldose redutase.
Applications Claiming Priority (2)
Application Number | Priority Date | Filing Date | Title |
---|---|---|---|
US201962912441P | 2019-10-08 | 2019-10-08 | |
PCT/US2020/054607 WO2021071965A1 (en) | 2019-10-08 | 2020-10-07 | Aldose reductase inhibitors for treatment of phosphomannomutase 2 deficiency |
Publications (1)
Publication Number | Publication Date |
---|---|
BR112022005895A2 true BR112022005895A2 (pt) | 2022-06-28 |
Family
ID=75437528
Family Applications (1)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
BR112022005895A BR112022005895A2 (pt) | 2019-10-08 | 2020-10-07 | Inibidores de aldose redutase para tratamento de deficiência de fosfomanomutase 2 |
Country Status (10)
Country | Link |
---|---|
US (1) | US20220226323A1 (pt) |
EP (1) | EP4041219A4 (pt) |
JP (1) | JP2022552831A (pt) |
CN (1) | CN114667139A (pt) |
AU (1) | AU2020363699A1 (pt) |
BR (1) | BR112022005895A2 (pt) |
CA (1) | CA3153108A1 (pt) |
IL (1) | IL291946A (pt) |
MX (1) | MX2022004270A (pt) |
WO (1) | WO2021071965A1 (pt) |
Families Citing this family (2)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
MX2020001057A (es) | 2017-07-28 | 2020-11-24 | Applied Therapeutics Inc | Composiciones y metodos para tratar la galactosemia. |
WO2024064147A1 (en) * | 2022-09-20 | 2024-03-28 | Mayo Foundation For Medical Education And Research | Treating congenital disorders of glycosylation |
Family Cites Families (5)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
WO2013123403A1 (en) * | 2012-02-15 | 2013-08-22 | Sanford-Burnham Medical Research Institute | Theranostics platform and methods of use |
HRP20231563T1 (hr) * | 2016-06-21 | 2024-03-15 | The Trustees Of Columbia University In The City Of New York | 4-okso-3,4-dihidrotino[3,4-d]piridazinski spojevi kao inhibitori aldosoreduktaze i načini njihove upotrebe |
MX2020001057A (es) * | 2017-07-28 | 2020-11-24 | Applied Therapeutics Inc | Composiciones y metodos para tratar la galactosemia. |
WO2020040831A1 (en) * | 2018-08-20 | 2020-02-27 | Perlara Pbc | Methods for treating congenital disorders of glycosylation |
BR112021019596A2 (pt) * | 2019-04-01 | 2021-11-30 | Applied Therapeutics Inc | Inibidores de aldose redutase |
-
2020
- 2020-10-07 CA CA3153108A patent/CA3153108A1/en active Pending
- 2020-10-07 CN CN202080070704.XA patent/CN114667139A/zh active Pending
- 2020-10-07 AU AU2020363699A patent/AU2020363699A1/en active Pending
- 2020-10-07 BR BR112022005895A patent/BR112022005895A2/pt unknown
- 2020-10-07 MX MX2022004270A patent/MX2022004270A/es unknown
- 2020-10-07 IL IL291946A patent/IL291946A/en unknown
- 2020-10-07 WO PCT/US2020/054607 patent/WO2021071965A1/en unknown
- 2020-10-07 JP JP2022521134A patent/JP2022552831A/ja active Pending
- 2020-10-07 EP EP20875044.8A patent/EP4041219A4/en active Pending
-
2022
- 2022-04-07 US US17/715,401 patent/US20220226323A1/en active Pending
Also Published As
Publication number | Publication date |
---|---|
IL291946A (en) | 2022-06-01 |
JP2022552831A (ja) | 2022-12-20 |
MX2022004270A (es) | 2022-05-03 |
CA3153108A1 (en) | 2021-04-15 |
EP4041219A4 (en) | 2023-11-01 |
WO2021071965A1 (en) | 2021-04-15 |
US20220226323A1 (en) | 2022-07-21 |
EP4041219A1 (en) | 2022-08-17 |
CN114667139A (zh) | 2022-06-24 |
AU2020363699A1 (en) | 2022-05-26 |
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